RARE News

RARE News

Rare Disease Day 2024 – Call for greater awareness of X-linked adrenoleukodystrophy and cerebral adrenoleukodystrophy

By admin

20 March 2024

RARE News

Rare disease advocates learn to accelerate therapeutic development at 9th RARE Drug Development Symposium

By admin

19 March 2024

RARE News

Alnylam launches Hereditary ATTR (hATTR) Amyloidosis campaign to help shorten diagnosis time

By admin

19 March 2024

RARE News

New primer highlights latest understanding of rare inherited disease alkaptonuria

By admin

19 March 2024

RARE News

DEBRA UK asks the British public to BE the difference for EB in 2024

By admin

19 March 2024

RARE News

Launching CamRARE’s ‘The Need for a RARE Patient Passport’ Report for Rare Disease Day

By admin

1 March 2024

RARE News

Coave Therapeutics Receives Grant from the ALS Association to Advance its CTx-TFEB Program as a Potential Treatment for All Forms of ALS

By admin

29 February 2024

RARE News

SMA Europe launches “Care for adults living with SMA in Europe: a benchmarking report.”

By admin

29 February 2024

RARE News

£1.5 million new fund launched to ‘Help the Heart’

By admin

27 February 2024

RARE News

CureDuchenne hosts “Champions in Miami” event on March 9 to help find a cure for Duchenne muscular dystrophy

By admin

23 February 2024

RARE News

CMT Research Foundation partners to advance study of CMT type 1J by Dr Stephan Zuchner

By admin

21 February 2024

RARE News

Patients as Partners in Clinical Research Conference 2024

By admin

19 February 2024

Charity & advocacy

Rare Disease Awareness Day Calendar

By CONTRIBUTOR

14 February 2024

RARE News

MEF2C Foundation & MUSC launch program to develop MEF2C therapeutics

By admin

9 February 2024

RARE News

National Tay-Sachs & Allied Diseases Association hosts first of its kind drug development meeting for GM2

By admin

2 February 2024

RARE News

Get Ready to #ShowYourStripes for Rare Disease Day 2024 29th February: the rarest day of the year!

By admin

1 February 2024

RARE News

CureDuchenne announces educational events for families and caregivers of individuals with Duchenne or Becker muscular dystrophy

By admin

31 January 2024

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